Beyond the Bench
Our research benefits patients and families living with Leigh syndrome and other mitochondrial diseases. For more information and support, please check out the sites below:
Cure Mito Fundation
Kasey Woleben established the Cure Mito foundation six years ago as Cure SURF1 Foundation because her son, Will, was diagnosed with SURF1 Leigh syndrome. We have been working together since then to help Will and other SURF1 patients to find hope through gene therapy. Kasey then changed the name of the foundation to Cure Mito Foundation to help other mitochondrial disease kids, including MTATP6.
Uplifting Athletes
Penn State University football player Scott Shirley established Uplifting Athletes in 2003. Since then, they have been sponsoring many rare disease research projects, including our gene therapy development for MTATP6.
NF Northeast
We thank NF Northeast for getting us started on the NF2 journey. Their foundation also supports research in more common NF1 diseases.
Cure NF2
NF2-related schwannomatosis causes devastating tumors on the nerves that control hearing, balance, and movement. There is no approved treatment. Cure NF2 Foundation funds cutting-edge gene therapy research and amplifies the voices of patients and families who refuse to give up.